News & Updates
FDA Approves Emcitate (Tiratricol): First Treatment for MCT8 Deficiency (Allan-Herndon-Dudley Syndrome)
On September 28, 2026, the US FDA approved Emcitate (tiratricol), the first treatment for MCT8 deficiency, also known as Allan-Herndon-Dudley ...
FDA Approves Isembyld (Apitegromab-mstn), First Muscle-Targeted Therapy for Spinal Muscular Atrophy
Families living with spinal muscular atrophy (SMA) have watched treatment options improve a lot over the last few years. But ...
FDA Approves First Drug to Treat Alexander Disease: Zanvastro (Zilganersen)
Alexander disease is one of those conditions where, until very recently, doctors could only offer supportive care and watch the ...
FDA Approves First Intranasal Diuretic, Enbumyst
Enbumyst (bumetanide nasal spray), developed by Corstasis Therapeutics, has received approval from the U.S. Food and Drug Administration (FDA). It ...
Moderna’s 2025–2026 COVID-19 Vaccines Receive FDA Approval
The 2025–2026 formulations of Moderna's COVID-19 vaccines, Spikevax® and mNexspike®, have received approval from the U.S. Food and Drug Administration ...
FDA Approves First-in-Class Therapy for Hereditary Angioedema
Dawnzera (Donidalorsen) is now approved by the U.S. Food and Drug Administration (FDA) as the first-ever and only therapy targeting ...
We’re Heading to ESMO Congress 2025 in Berlin
We’re pleased to confirm our participation at the ESMO Congress 2025 in Berlin, Germany, one of the most important oncology ...
Takeda’s Qdenga Vaccine: A Breakthrough in Dengue Prevention Coming to India
Takeda Pharmaceuticals recently declared its plans to launch Qdenga, its dengue vaccine, in India by next year. This vaccine could ...
Indian Company Can Manufacture Risdiplam for Spinal Muscular Atrophy (SMA)
In a major development, a leading Indian pharmaceutical company, Natco Pharma, has been given approval to produce Risdiplam. This is ...